@article{jablonka2022-34983696, author = {Jablonka, S. and Hennlein, L. and Sendtner, M.}, title = {{Therapy development for spinal muscular atrophy: perspectives for muscular dystrophies and neurodegenerative disorders}}, journal = {Neurological research and practice}, year = {2022}, doi = {10.1186/s42466-021-00162-9}, pmid = {34983696}, url = {https://doi.org/10.1186/s42466-021-00162-9} }