@article{tran2022-34949835, author = {Tran, H. and Moazami, M. P. and Yang, H. and McKenna-Yasek, D. and Douthwright, C. L. and Pinto, C. and Metterville, J. and Shin, M. and others}, title = {{Suppression of mutant C9orf72 expression by a potent mixed backbone antisense oligonucleotide}}, journal = {Nature medicine}, year = {2022}, doi = {10.1038/s41591-021-01557-6}, pmid = {34949835}, url = {https://doi.org/10.1038/s41591-021-01557-6} }